Nitisinone
Nitisinone is a hydroxyphenylpyruvate dioxygenase inhibitor used as an adjunct to dietary restrictions for the treatment of hereditary tyrosinemia type 1 (HT-1), which causes intolerance to tyrosine containing foods.
Systematic name
2-[2-nitro-4-(trifluoromethyl)benzoyl]cyclohexane-1,3-dione
Therapeutic category
Hereditary tyrosinemia
Available formulations
Solid