Vanzacaftor
Vanzacaftor is a novel CFTR (Cystic fibrosis transmembrane conductance regulator) corrector.
Systematic name
(14S)-8-[3-(2-dispiro[2.0.24.13]heptan-7-ylethoxy)pyrazol-1-yl]-12,12-dimethyl-2,2-dioxo-2λ6-thia-3,9,11,18,23-pentazatetracyclo[17.3.1.111,14.05,10]tetracosa-1(22),5(10),6,8,19(23),20-hexaen-4-one
Therapeutic category
Cystic fibrosis
Available formulations
N/A